Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...
Saffie Sandford was born with Leber's Congenital Amaurosis and "missed out on a lot" due to difficulties seeing in any ...
An experimental gene therapy for a rare form of genetic deafness has successfully restored hearing in children and adults, ...
A first-of-its-kind gene therapy that can restore hearing in children born deaf has just cleared its final hurdle—and, in a ...
Danish dermatology specialist Leo Pharma is paying $50 million for U.S. gene writing biotech Replay and its preclinical gene ...
The agency's decision is based on results from a clinical trial in which the treatment improved hearing in 80 percent of the ...
Astellas Pharma has done some spring cleaning of its pipeline, dropping two phase 1 candidates and slamming the brakes on a ...
A medical field that almost died is quietly fixing one disease at a time.
Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have ...
Kelly Anne is a deputy editor at Forbes Advisor overseeing the development of various initiatives, including newsletters, ...
Sean Davies has a rare inherited form of MND and says he has benefited from specialist treatment.
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