Researchers described a promising new approach for using gene therapy to treat sickle cell disease in the peer-reviewed journal Human Gene Therapy. To improve the efficacy of gene therapy when using ...

Two papers published in The New England Journal of Medicine highlight the potential of gene editing for treatment of sickle ...

A major step forward in treating inherited blood disorders in Qatar Sidra Medicine a member of Qatar Foundation is now ...

Sickle cell disease affects between 12,500 and 15,000 people in England. Ezume Images/ Shutterstock A drug that can treat severe sickle cell disease has recently been given approval by the National ...

Promising results from the first clinical trials of globin gene transfer to treat beta-thalassemias-inherited forms of anemia-have eliminated the need for blood transfusions in some individuals.

Key takeawaysResults from a UCLA-led clinical trial for sickle cell disease reveal the unique challenges of treating blood disorders with gene therapy ...

Gang Bao is Rice University's A.J. Foyt Family Professor of Bioengineering, professor of chemistry, materials science and nanoengineering and mechanical engineering, Cancer Prevention and Research ...

Researchers developed a new gene-editing strategy that dramatically boosts the effectiveness of gene therapies in the liver, a breakthrough that could lead to new treatments for about 700 genetic ...